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lonafarnibCareFirst (Caremark)

Processing-Deficient Progeroid Laminopathy with Progerin-Like Protein Accumulation

Initial criteria

  • Member is age ≥ 12 months
  • Member has a body surface area ≥ 0.39 m2
  • Diagnosis of Processing-Deficient Progeroid Laminopathy is confirmed with genetic testing indicating a heterozygous LMNA pathogenic variant
  • Medication is prescribed by or in consultation with a physician who specializes in metabolic disease and/or lysosomal storage disorders

Reauthorization criteria

  • Member meets all initial authorization criteria
  • Member is experiencing benefit from therapy

Approval duration

12 months