Zokinvy (lonafarnib) — Point32Health
Processing-deficient Progeroid Laminopathies
Initial criteria
- Documented diagnosis of processing-deficient Progeroid Laminopathies
- The patient is age ≥ 12 months
- Prescribed by or in consultation with a specialist in progeria, genetics, or metabolic disorders
- Documented body surface area ≥ 0.39 m²
- Documentation of one of the following: heterozygous LMNA mutation with progerin-like protein accumulation OR homozygous or compound heterozygous ZMPSTE24 mutations