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Aqneursa (levacetylleucine)United Healthcare

neurological manifestations of Niemann-Pick disease type C (NPC)

Initial criteria

  • Diagnosis of Niemann-Pick disease type C (NPC)
  • Aqneursa is being used to treat neurological manifestations of NPC
  • Patient is not receiving Aqneursa in combination with Miplyffa (arimoclomol)

Reauthorization criteria

  • Documentation of positive clinical response to Aqneursa (e.g., slowed disease progression from baseline based on assessment with NPC–specific scales)
  • Patient is not receiving Aqneursa in combination with Miplyffa (arimoclomol)

Approval duration

12 months