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Opfolda (miglustat)United Healthcare

late-onset Pompe disease

Initial criteria

  • Diagnosis of late-onset Pompe disease
  • AND
  • Patient has an active UnitedHealthcare medical benefit prior authorization for Pombiliti (cipaglucosidase alfa-atga) for the treatment of late-onset Pompe disease

Reauthorization criteria

  • Documentation of positive clinical response to Opfolda plus Pombiliti
  • AND
  • Opfolda continues to be prescribed in combination with Pombiliti

Approval duration

12 months