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Palynziq (pegvaliase-pqpz)United Healthcare

phenylketonuria (PKU)

Initial criteria

  • Diagnosis of phenylketonuria (PKU)
  • AND Patient has a blood phenylalanine concentration greater than 600 micromol/L
  • AND Patient is actively on a phenylalanine-restricted diet
  • AND Patient is not receiving Palynziq in combination with sapropterin dihydrochloride

Reauthorization criteria

  • Documentation of positive clinical response (e.g., blood phenylalanine concentration less than 600 micromol/L, 20% reduction in blood phenylalanine concentration from pretreatment baseline)
  • AND Patient is actively on a phenylalanine-restricted diet
  • AND Patient is not receiving Palynziq in combination with sapropterin dihydrochloride

Approval duration

12 months