Zokinvy (lonafarnib) — United Healthcare
Processing-deficient progeroid laminopathies
Initial criteria
- Diagnosis of processing deficient progeroid laminopathy
- AND
- Documentation of one of the following:
- i. Heterozygous LMNA mutation with progerin-like protein accumulation
- OR
- ii. Homozygous or compound heterozygous ZMPSTE24 mutations
Approval duration
12 months